Adeno-Associated Virus-Based Gene Therapy for CNS Diseases
نویسندگان
چکیده
منابع مشابه
Adeno-Associated Virus-Based Gene Therapy for CNS Diseases
Gene therapy is at the cusp of a revolution for treating a large spectrum of CNS disorders by providing a durable therapeutic protein via a single administration. Adeno-associated virus (AAV)-mediated gene transfer is of particular interest as a therapeutic tool because of its safety profile and efficiency in transducing a wide range of cell types. The purpose of this review is to describe the ...
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ژورنال
عنوان ژورنال: Human Gene Therapy
سال: 2016
ISSN: 1043-0342,1557-7422
DOI: 10.1089/hum.2016.087